KEI Briefing Note 2020:4 Selected Government Definitions of Orphan or Rare Diseases

KEI Briefing Note 2020:4 Selected Government Definitions of Orphan or Rare Diseases
Revised October 28, 2020
Arianna Schouten

Table 1: Country Definitions of Orphan or Rare Diseases
Table 2: Patients per 100,000

PDF available here: KEI-Briefing-Note-2020-4-Defining-Rare-Diseases